Morbus Pompe
Laufzeit: 01.01.2017 - 31.12.2017
imported
Kurzfassung
A phase 3 randomized, multicenter, multinational, double-blinded study comparing the efficacy and safety of repeated biweekly infusions of NeoGAA (GZ402666) and alglucosidase alfa in treatment naïve patients with late onset Pompe disease