Efficacy and safety of Velmanase alfa in the treatment of patients with alpha-mannosidosis: results from the core and extension phase analysis of a phase III multicentre, double-blind, randomised, placebo-controlled trial
JOURNAL OF INHERITED METABOLIC DISEASE. Bd. 41. H. 6. 2018 S. 1215-1223
Erscheinungsjahr: 2018
Publikationstyp: Zeitschriftenaufsatz
Geprüft | Bibliothek |
Autoren
Borgwardt, Line (Autor)
Guffon, Nathalie (Autor)
Amraoui, Yasmina (Autor)
Dali, Christine I. (Autor)
De Meirleir, Linda (Autor)
Gil-Campos, Mercedes (Autor)
Heron, Benedicte (Autor)
Geraci, Silvia (Autor)
Ardigo, Diego (Autor)
Cattaneo, Federica (Autor)
Fogh, Jens (Autor)
Van den Hout, J. M. Hannerieke (Autor)
Beck, Michael (Autor)
Jones, Simon A. (Autor)
Tylki-Szymanska, Anna (Autor)
Haugsted, Ulla (Autor)
Lund, Allan M. (Autor)
Klassifikation
DDC Sachgruppe:
Medizin